*A motor milestone responder was defined according to the Hammersmith Infant Neurological Examination (HINE) Section 2: ≥2 point increase (or maximal score) in ability to kick, or ≥1-point increase in the motor milestones of head control, rolling, sitting, crawling, standing or walking, and improvement in more categories of motor milestones than worsening.1
age 9*Later-onset (Type III) SMA
treated with SPINRAZA®
~5.5 years as of 9/18
1. SPINRAZA® Summary of Product Characteristics.