An open-label, re-dosing extension study in patients who previously participated in clinical studies of SPINRAZA® (ENDEAR, CHERISH, EMBRACE, CS12* or CS3a)1
Patients are diagnosed with infantile-onset (Type I) or later-onset (Type II/III) SMA1
All patients in SHINE are receiving SPINRAZA® 12-mg1
The study is ongoing
*Study CS12 involved re-dosing patients who had previously participated in studies CS1, CS2 and CS10.
Bill age 48*Later-onset (Type III) SMA treated with SPINRAZA®
*Age at time of photo shoot.
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